More information:
Johnny Mahlangu et al, Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A, New England Journal of Medicine (2023). DOI: 10.1056/NEJMoa2211075
Lindsey A. George, Hemophilia A Gene Therapy—Some Answers, More Questions, New England Journal of Medicine (2023). DOI: 10.1056/NEJMe2212347