How AI can help in gene delivery vector discovery and design :hmn
Genome engineering and gene therapies that manipulate DNA sequences in cells have driven a biotechnological revolution over the past decade.1 Adeno-associated virus (AAV) vectors are the leading platform for in vivo gene delivery for the treatment of various human diseases. Alipogene tiparvovec and voretigene neparvovec-rzyl, two recombinant AAV-based gene therapy products, were approved by the …