Impact of imiglucerase supply constraint on the therapeutic management and course of disease in French patients with Gaucher disease type 1
1 Department of General Internal Medicine, Geneva University Hospital, Rue Gabrielle-Perret-Gentil 4, Genève 14, CH-1211, Switzerland
2 Department of Oncology and Hematology, Saint Vincent de Paul Hospital, Nord de France University, Lille, France
3 Department of Internal Medicine, Fondation Saint Joseph Hospital, Marseille, France
4 Department of hematology, Morvan Hospital, CHRU, Brest, France
5 Department of Internal Medicine, Croix Saint Simon Hospital, Paris, France
6 Department of Internal Medicine, CHU Nantes, Nantes, France
7 Clinical Immunology and Osteoarticular Diseases Therapeutic Unit, CHRU, Lapeyronie, Montpellier, France
8 Medical Department, Genzyme SAS, Saint Germain en Laye, France
9 Referral Center for Lysosomal Diseases and Department of Internal Medicine, CHU Paris Nord Val de Seine, Clichy, France