The TREAT-NMD advisory committee for therapeutics (TACT): an innovative de-risking model to foster orphan drug development
1 Newcastle University, Newcastle upon Tyne, UK
2 Cydan Developments Inc, Cambridge, USA
3 Pharma Mac, Boca Grande, USA
4 Children’s National Medical Center, Washington, USA
5 Johns Hopkins University, Baltimore, USA
6 Genethon, Evry, France
7 University of Freiburg, Freiburg, Germany
8 Nationwide Children’s Hospital, Columbus, USA
9 National Institutes of Health, Washington, USA
10 Parent Project Muscular Dystrophy, New Jersey, USA
11 Royal Veterinary College, London, UK